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RNA Editing for Muscular Dystrophy Therapy© 2016, Springer Science+Business Media New York.Due to lack of effective therapies, muscular

Pre- and posttranscriptional genetic information modification in muscular dystrophy treatment groups of genetic pathologies is musculardystrophy, including such diseases as Duchenne muscular

Gene- and cell-based therapy of muscle system hereditary disorders: State-of-artDuchenne muscular dystrophy

Pre- and posttranscriptional genetic information modification in muscular dystrophy treatment groups of genetic pathologies is musculardystrophy, including such diseases as Duchenne muscular

Gene- and cell-based therapy of muscle system hereditary disorders: State-of-artDuchenne muscular dystrophy

RNA Editing for Muscular Dystrophy Therapy© 2016, Springer Science+Business Media New York.Due to lack of effective therapies, muscular

RNA Editing for Muscular Dystrophy TherapyDue to lack of effective therapies, muscular dystrophies became a focus for gene therapy. Multiple

Therapeutic potential of highly functional codon‑optimized microutrophin for muscle‑specific expression of dystrophin (μDys) for Duchenne muscular dystrophy (DMD), with several drug candidates currently undergoing

Sarcoglycanopathies: Clinical, Molecular and Genetic Characteristics, Epidemiology, Diagnostics and Treatment Options symptoms of sarcoglycanopathies resemble the ones in Duchenne/Becker muscular dystrophy and several

Genetics of cardiomyopathies [Genetika kardiomiopatii.]muscular dystrophy

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